Jacob Borrajo
Founder & Chief Executive Officer Amber Bio
Seminars
Wednesday 30th July 2025
Programmable Multi-Kilobase RNA Editing with Splice Editors
1:00 pm
• Amber Bio is building Splice Editors, a novel RNA editing technology
• Exploring the ways Splice Editors can achieve multi-kilobase edits with a single AAV
• Understanding how Splice Editors open the aperture for addressable targets
Thursday 31st July 2025
Panel Discussion: Uncovering Differentiated Targets, Exploring Editing in a Wider Range of Diseases & Identifying Patients Who Could Benefit from RNA Editing
2:30 pm
• Identifying differentiated target sequences using human genomics data and AI
• Exploring editing ceilings and limitations of various targets
• Elucidating treatable diseases and identifying patients with the suitable genotype who could benefit from treatment
