Novel Delivery Strategies for More Durable & Potent RNA Editing Machinery
RNA editing therapeutics have great potential in treating a brand-new landscape of diseases due to its transient effects, however, it is currently plagued by difficult delivery to target tissues. With the possibility of modifying guide RNA, this session will uncover the unique delivery platforms which can be utilized to enable targeting of specific tissues, considering the capabilities of conjugates for specifically targeting RNA and reviewing opportunities of delivery beyond LNPs to enable repeatable dosing for more long-lasting and safer effects.